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Rare Disease Conference 2024 - Rare Disease Summit
March 19-21, 2024
Pre-Conference Workshops on March 18, 2024Philadelphia Marriott Downtown | Philadelphia, PA


The Rare Disease Summit is hosted on Streamly, Informa's new video platform.

Streamly provides insight and analysis from the world’s leading experts, direct to your screen. Dive into Informa's rich network of specialists and search, skip and bookmark the videos you need to stay one step ahead.

Built with advanced search functionality and user experience that's made with you in mind.


What is Streamly?

As well as offering world-class video insights from across the industry, Streamly is also the official platform to catch up on the Rare Disease Summit wherever and whenever suits you.

Streamly makes it easy to find the sessions you may have missed during the event, or rewatch those you loved. The website lets you search by speaker, title of the presentation, company name or even find content that contains a buzzword that might be of interest to you.

Never miss a session again!

How do I access the Rare Disease Summit videos?

If you attend the Rare Disease Summit in 2023, you will get access to the content on-demand after the event.

If you have logged into Streamly or an Informa Connect account before, you may use your previous password, or reset it using "Forgotten your password" to create a new one.

Having trouble? Contact

World class insights from experts: Rare Disease Summit 2023

Streamly gives you access to a library of top-level contributors discussing the latest trends affecting your industry.

Nowhere else will you will hear from so many leading thought leaders, including representatives from organizations such as Alexion Pharmaceuticals: AstraZeneca Rare Disease, Angelman Syndrome Foundation, American College of Medical Genetics and Genomics, Axonis Therapeutics, Bayer Oncology, Black Women's Health Imperative, Blueprint Medicines, Calliditas Therapeutics, Canary Advisors, Cognito Therapeutics, Collaborations Pharmaceuticals, COMBINEDBrain, Cornerstone Pharmaceuticals, Cytokinetics, DDX3X Foundation, Duke-Robert J. Margolis, MD, Center for Health Policy, Dup15q Alliance, Enzyvant Therapeutics, EURORDIS - Rare Disease Europe, Forge Biologics, Foundation for Scardosis Research, Horizon Therapeutics, Igia Pharmaceuticals, Janssen Pharmaceutical Companies of Johnson & Johnson, Jazz Pharmaceuticals, Kinevant Sciences, Lantern Pharma, MorphoSys, Nanoscope Therapeutics, NS Pharma, Orange County Free Clinic, Orsini Healthcare, PeopleMetrics, Pharming Healthcare, PTC Therapeutics, Rare Patient Voice, RARE Regeneron, Revolution, Sanofi, Sparing Vision, Sudo BioSciences, Takeda, To Cure a Rose Foundation, Tonix Pharmaceuticals, U.S. Food and Drug Administration, WEP Clinical, Xontogeny LLC and more.

Get even more insights on rare disease access, innovation and beyond

Buy events on-demand - Coming Soon

Soon you will be able to purchase on-demand event videos from conferences you might have missed in the past and future conferences you may not be able to attend in person.

Explore a wide range of freely available Streamly videos

With hundreds of videos from bite-size explainers to exclusive in-depth interviews with global thought leaders, Streamly helps you to stay ahead of the conversation in your industry. Already live, Streamly covers some of the biggest knowledge areas with Marketing, Fintech, Insights and Innovations as well as Sustainability, Leadership and many more coming soon.