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Rare Disease Innovation & Partnership Summit
March 21-23, 2023
Delivered as a Hybrid EventPhiladelphia Marriott Downtown

Connect Key Stakeholders to Drive Therapeutic Progress, Propel Commercial Strategies and Inspire Impactful Advocacy

Generate solution-focused strategies surrounding patient access, reimbursement, commercialization, launch, partnering and more. Join experts from across the rare disease community to unite in areas of unmet medical need and create life-transforming therapies and breakthroughs.

What's Coming Your Way in 2023?

Novel Approaches to High-Impact Topics:

  • Integrating Racial Disparity into the Rare Disease Conversation
  • Identifying Rare Disease Patients - Finding a Needle in a Haystack
  • Setting Yourself Up for Success - Best Practices for a Successful Product Launch
  • Shifting the Focus: Patient Centered Outcome Measures
  • Modernizing the System to Sustain Newborn Screening
  • Strengthening Relationships: Putting the Patient in the Driver’s Seat

Riveting Keynotes and Panels Deliver Fresh Perspectives:

  • Navigate FDA Updates on Rare Disease Product Development
  • How to Promote Growth during Uncertain Times: When will the Biotech Pendulum Swing Again?
  • Furthering Insights on FDA Guidance - Patient Focused Drug Development Series
  • Overcoming Investment Challenges in the Rare Disease Space
  • Uncovering Access to Genomic Sequencing

Customize Your Agenda with Focused Breakouts, Including Key Topic Areas:

  • Patient-Driven Progress - Driving models to advancing company formation, advocacy and drug development led by patients and disease foundations
  • Reimbursement, Value and Access - Evolving pricing, value-based payment and reimbursement trends impacting market and patient access to orphan products
  • New Launch and Commercialization - Critical strategies and commercialization frameworks for launching products within the rare disease market
  • Partnering, Investment and Portfolio Strategy - Opportunities for collaboration, value growth drivers and funding inflection points to propel innovation

Who should attend

You will benefit from attending this event if you work for a company that focuses on rare disease and orphan drugs and have responsibilities or involvement in the following areas:

  • Market Access
  • Rare Disease
  • Orphan Drugs
  • Commercial Strategy/Operations
  • Reimbursement
  • Early/Expanded Access
  • Launch Excellence
  • Product Launch
  • Portfolio Management/Strategy
  • Marketing
  • Development
  • Patient Advocacy
  • Payer Strategy
  • Patient Support/Services

This event will also benefit consultants and solution providers who provide services in the rare disease space.


Connect and Network with Key Decision-Makers at the Rare Disease Summit

Whether you’re looking to generate quality leads, showcase thought leaders, or reinforce your brand, collaborate with us to identify custom sponsorship opportunities to help you reach your business objectives.

For more information about custom opportunities to reach a qualified audience, please contact us here.

Vice President

Regulatory Affairs, North America

Sobi, Inc.

I thought this was one of the best conferences I’ve attended over the years. The focus was very practical and each speaker shared real world examples instead of theory. It was well organized and the passion each participant has for helping people with rare disease was very evident.