Key Sessions
Marie Wikstrom-Lindholm
Keynote Panel: The Potential of RNA Therapeutics – Rare vs Chronic Applications
Silence Therapeutics
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Main Conference – Day 1 - CET (Central European Time, GMT+01:00)
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Main Conference – Day 1 - CET (Central European Time, GMT+01:00)
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Business Forum: Rapid-Fire Innovation Session
11:30 - 11:45
Innovation Presentation: MEVs: A Versatile Delivery Platform for Advanced Therapeutics, Vaccines, and Gene Therapies
- Extracellular vesicles derived from microalgae (MEVs) are being developed as a universal delivery system for therapeutics, vaccines, and gene therapies.
- MEVs demonstrate high performance, safety, and flexibility in delivering diverse payloads, including mRNAs, siRNAs, oligos, plasmids, peptides, and proteins. They can be administered through various non-invasive routes, such as topical, ocular, oral, respiratory, intranasal, intramuscular, and intravenous, enabling delivery to hard-to-reach tissues while addressing limitations of existing delivery systems.
- MEV manufacturing is sustainable, simple, cost-effective, and GMP-ready. Production relies on environmentally friendly processes using light, fresh water, and minerals, ensuring a green and scalable approach.
11:45 - 12:00
Innovation Presentation: Rewriting genes – RNA editing platform development
- Splice Editors increase trans-splicing efficiency by leveraging CRISPR-Cas systems
- Splice Editor-enabled multi-kilobase edits unlock several key indications and pathogenic variants
- Splice Editing is a promising new modality for RNA editing
- Jacob Borrajo - CEO, Amber Bio
12:00 - 12:15
Innovation Presentation: Novel RNA splicing modulation platform targeting pseudo-exons
- Developing an innovative RNA splicing modulation platform to selectively target pseudo-exons, addressing genetic mutations that lead to aberrant splicing and disease progression.
- Leveraging advanced technologies to restore normal splicing patterns, enabling precise therapeutic interventions for a range of genetic disorders with high unmet medical needs.
- Poul Sørensen - CEO, Inverna therapeutics
12:15 - 12:30
Innovation Presentation:
Please contact the RNA Leaders Team (jade.osei-tutu@informa.com) if you are interested in presenting
12:30 - 12:45
Innovation Presentation:
Please contact the RNA Leaders Team (jade.osei-tutu@informa.com) if you are interested in presenting
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