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Day 3: Main Conference
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Day 3: Main Conference
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07:30 - 08:0030 mins
Morning Spotlight Presentation
Novel Ionizable Lipid Library for Enabling Non-Viral Delivery
- Martin Rabel, PhD - Senior Field Application Scientist, Precision NanoSystems
08:10 - 08:155 mins
Oligonucleotide Discovery, Preclinical and Clinical
Chairperson’s Remarks
- Troels Koch, PhD - Senior Vice President, Chemistry; MiNa therapeutics, MiNa Therapeutics
08:10 - 08:155 mins
Peptide Chemistry, Manufacturing and Controls
Chairperson's Remarks
- Franziska Arnhold, PhD - Director, Business Development, Bachem AG
08:10 - 08:155 mins
mRNA Discovery, Preclinical and Clinical
Chairperson's Remarks
- Christoph Kroener - Director DNA Process Development & Cap Technology, BioNTech AG
08:15 - 08:4530 mins
Oligonucleotide Discovery, Preclinical and Clinical
RNA Therapeutics Modalities and Targeted Delivery Approaches for Developing Transformational Medicines for Patients
- Tamar Grossman, PhD - VP, Global Head of RNA & Targeted Therapeutics, Janssen Pharmaceutical Companies of John
08:15 - 08:4530 mins
Peptide Chemistry, Manufacturing and Controls
New Tools for Chemoselective Disulfide Formation in Cysteinyl Peptides
- Fernando Albericio, PhD - Research Professor, School of Chemistry, University of Kwazulu-Natal
08:15 - 08:4530 mins
mRNA Discovery, Preclinical and Clinical
Development of Broadly Protective Influenza Vaccines Using Necleoside-Modified mRNA
- Norbert Pardi, PhD - Assistant Professor, University of Pennsylvania
08:45 - 09:1530 mins
Oligonucleotide Discovery, Preclinical and Clinical
GalAhead™: A Novel Therapeutic GalNAc-RNAi Platform to Downregulate Single and Multiple Genes
- Dmitry Samarsky, PhD - Chief Technology Officer, Sirnaomics
08:45 - 09:1530 mins
Peptide Chemistry, Manufacturing and Controls
Technology Transfer of Multi Peptides - A Case Study
- Pierre-Emmanuel Broutin, PhD - Project Chemist, Polypeptide Group
08:45 - 09:1530 mins
mRNA Discovery, Preclinical and Clinical
mRNA Therapeutics for Treatment of Liver Fibrosis
- Wolfgang Grosse, PhD - Associate Director Protein Design, CureVac AG
09:15 - 09:4530 mins
Oligonucleotide Discovery, Preclinical and Clinical
Oligonucleotide Chemistry and Delivery
- Jayaprakash Nair, PhD - Senior Director, Chemistry and Delivery Science, Alnylam Pharmaceuticals
09:15 - 09:4530 mins
Peptide Chemistry, Manufacturing and Controls
Dasiglucagon The Journey from Compound to Commercial Product
- Frederik Barfoed Beck, PhD - Senior Outsourcing Manager, Zealand Pharma A/S
09:15 - 09:4530 mins
mRNA Discovery, Preclinical and Clinical
Update on Personalized Cancer Therapy Using messenger RNA
- Christoph Kroener - Director DNA Process Development & Cap Technology, BioNTech AG
09:45 - 10:3045 mins
Networking Refreshment Break in Poster and Exhibit Hall
10:30 - 11:0030 mins
Oligonucleotide Discovery, Preclinical and Clinical
Towards a Stereo Defined mRNAi Trigger: Phosphordithioates Avoid Undefined Stereo Centres in GalNAc-conjugated siRNA
- Lucas Bethge - Vice President and Group Leader Oligonucleotide Chemistry, Silence Therapeutics
10:30 - 11:0030 mins
Peptide Chemistry, Manufacturing and Controls
A Cocktail of Multi PEGylated Peptides - A Case Study in Peptide GMP Process Development
- Audrey Parat, PhD - Project Chemist, PolyPeptide Group
10:30 - 11:0030 mins
mRNA Discovery, Preclinical and Clinical
EL-201: a systemic mRNA LNP Vaccine for the Treatment of HPV16+ Cancers
- Stefaan De Koker, PhD - Vice President, Discovery, eTheRNA Immunotherapies
11:00 - 11:3030 mins
Oligonucleotide Discovery, Preclinical and Clinical
Oligonucleotide Therapeutics for Duchenne Muscular Dystrophy: Current Developments and Competition from Alternative Approaches
- Thomas Roberts, DPhil - Senior Research Scientist, Research Fellow and Gro, University of Oxford
11:00 - 11:3030 mins
Peptide Chemistry, Manufacturing and Controls
Green Solid-Phase Peptide Synthesis: From Idea to Phase 3 Production
- Daniel Sejer Pedersen, PhD - Chemical Development Specialist, Novo Nordisk
11:00 - 11:3030 mins
mRNA Discovery, Preclinical and Clinical
Modulation of Host Immunity in the Airways with Interferon Lambda Encoding mRNA
- Christian Plank, PhD - Chief Technology Officer, Ethris GmbH
11:35 - 12:0530 mins
Spotlight Presentation 1
Explainable AI to Accelerate Life Sciences and Drug Discovery
- Marco Salvatore, PhD - Head of Bioinformatics, Target + Biomarker Discovery, Abzu
11:35 - 12:0530 mins
Spotlight Presentation 2
A Single-Use Disposable Tray for Bulk Lyophilization of Polypeptides and Oligonucleotides
- Scott Ross - Global Product Specialist, W.L. Gore & Associates
11:35 - 12:0530 mins
Spotlight Presentation 3
Designing Oligonucleotide Separations Using Reverse Phase Resins
- Martin Deetz, PhD - Technical Laureate, DuPont
12:05 - 13:2580 mins
Networking Luncheon in Poster and Exhibit Hall
13:25 - 13:5530 mins
Spotlight Presentation 1
A Modern and Efficient Solution for Oligonucleotide Analysis
- Chris Knowles, PhD - Senior Application Scientist, Waters
13:25 - 13:5530 mins
Spotlight Presentation 2
Demystifying Oligonucleotides: From R&D to Process scale, QA/QC to Manufacturing
- Rebecca Konietzny - Biopharma Specialist, Manager Technical Coverage and Solution Team EMEA, Agilent Technologies
- Beth Morgan - Head of Biopharma and Chemistries Business Development EMEAI, Agilent Technologies
13:25 - 13:5530 mins
Spotlight Presentation 3
Creating a Comprehensive Toolbox for Oligonucleotide Drug Discovery and Development
- Lijuan Pang, PhD - Project Director, Discovery Services, WuXi AppTec
13:55 - 14:005 mins
Oligonucleotide Discovery, Preclinical and Clinical
Chairman's Remarks
- Meena Meena, Ph.D. - Vice President of Bioanalytical, DMPK and Biomarker Development, Stoke Therapeutics
13:55 - 14:005 mins
Peptide Chemistry, Manufacturing and Controls
Chairman's Remarks
- Mimoun Ayoub, Ph.D. - Vice President, Global Head Sales and Key Account Management, CordenPharma International
13:55 - 14:005 mins
mRNA Discovery to Manufacturing
Chairman's Remarks
- David Estape - Senior Fellow, CRB Group
14:00 - 14:3030 mins
Oligonucleotide Discovery, Preclinical and Clinical
Progress on Development of RNA Base Editing Technologies for Precision Medicines
- Gerard Platenburg, PhD - Chief Scientific Officer, ProQR Therapeutics
14:00 - 14:3030 mins
Peptide Chemistry, Manufacturing and Controls
Aspen’s Green Continuous LPPS Method for the Manufacturing of Lanreotide: Control Strategy Considerations
- Ivo Eggen, PhD - Section Lead New Product Development, Aspen Oss B.V.
14:00 - 14:3030 mins
mRNA Discovery to Manufacturing
Preclinical Safety and Efficacy Studies of mRNA Vaccine STP2104 Against SARS-CoV
- Joo-Sung Yang - Vice President and Head of mRNA R&D, ST Pharm
14:30 - 15:0030 mins
Oligonucleotide Discovery, Preclinical and Clinical
CIVI 008: An Orally Active LNA Drug Against PCSK9
- Henrik Oerum, PhD - Founder and Chief Scientific Officer, CiVi Biopharma Inc.
14:30 - 15:0030 mins
Peptide Chemistry, Manufacturing and Controls
Refractometry to Study the Kinetics of the Solid-Phase Peptide Synthesis Process
- Beatriz De La Torre, Ph.D. - Research Professor, Laboratory of Medicine and Med, University Of KwaZulu-Natal
- John Lopez, PhD - Senior Expert Science & Technology, Novartis AG
14:30 - 15:0030 mins
mRNA Discovery to Manufacturing
Unlocking the Power of mRNA: Strategies for Manufacturing & Purification
- Carla Eller - MSAT Biomanufacturing Engineer, Merck KGaA
15:00 - 15:3030 mins
Oligonucleotide Discovery, Preclinical and Clinical
Non-clinical and Early Clinical Progress with STK-001, A Potential Disease Modifying Therapy for Dravet Syndrome
- Meena Meena, Ph.D. - Vice President of Bioanalytical, DMPK and Biomarker Development, Stoke Therapeutics
15:00 - 15:3030 mins
Peptide Chemistry, Manufacturing and Controls
Exploration of PAT & Continuous Flow Applications in Peptide Synthesis
- Andreas Heindl, PhD - Research Scientist, Peptide Synthesis and Process, Corden Pharma
15:00 - 15:3030 mins
mRNA Discovery to Manufacturing
Challenges and Current Approaches Concerning RNA Analytics for mRNA Therapeutics and Vaccines
- Simon Klenk, PhD - Director RNA Analytics, BioNTech SE
15:30 - 16:0030 mins
Networking Refreshment Break in Poster and Exhibit Hall
16:00 - 16:3030 mins
Oligonucleotide Discovery, Preclinical and Clinical
Circular RNA Aptamers as Therapeutics for Targeting Intracellular Proteins
- Jacob Litke, PhD - Chief Scientific Officer & Co-Founder, Chimerna Therapeutics
16:00 - 16:3030 mins
Peptide Chemistry, Manufacturing and Controls
Process Development of an Efficient Large-Scale Manufacturing Process of a PEG-ylated Peptide: Pegcetacoplan
- Arne Berthelmann, PhD - Director R&D, Bachem AG
16:00 - 16:3030 mins
mRNA Discovery to Manufacturing
Efficient mRNA Development and Manufacturing – Key Considerations and Best Practices
- Aditi Mehta, PhD - Senior Manager, Head of mRNA Process & Delivery, Merck KGaA
16:30 - 17:0030 mins
Oligonucleotide Discovery, Preclinical and Clinical
Drugging the Genome™ with Precision Genetic Medicines: Developing PNAs into Biotherapeutics
- Dietrich Stephan, Ph.D. - Chairman and CEO, NeuBase Therapeutics, Inc.
16:30 - 17:0030 mins
Peptide Chemistry, Manufacturing and Controls
A Hybrid Liquid Phase Peptide Synthesis (LPPS) Facility
- Rick Spencer - Senior Advisor - Process Engineering, Eli Lilly Kinsale
16:30 - 17:0030 mins
mRNA Discovery to Manufacturing
Will mRNA Redefine the Bio-manufacturing of the Future?
- David Estape - Senior Fellow, CRB Group
17:00 - 18:0060 mins
Close of Conference
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