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RNA Leaders USA
RNA breakthroughs, Case Studies and Partnerships
September 23-25, 2026Hynes Convention Center
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Thursday, September 24 - EST (Eastern Time, UTC-05:00

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Thursday, September 24 - EST (Eastern Time, UTC-05:00
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Showing 1 of 1 Streams
7:30am - 8:30am
Breakfast & Registration
Showing 3 of 3 Streams
8:30am - 8:35am
Chair Remarks
8:35am - 9:00am
Presentation: Computational Design of miR-128 Antisense Oligonucleotides for Post–MI Heart Failure
  • Anders Näär - Professor of Metabolic Biology, UC Berkeley
9:00am - 9:25am
Presentation: Custom Antisense Therapy GBFsen for familial ALS
  • Tamar Grossman - CEO, La Jolla Labs
9:25am - 9:50am
Presentation: n=1, expanding individualised RNA therapies for rare genetic diseases
  • Konstantina Skourti-Stathaki - Senior Director, ASO Discovery and Research, n-Lorem Foundation
9:50am - 10:15am
Presentation: Technology Presentation Opportunity Available

Please contact Jennifer Wickett for more information: Jennifer.Wickett@informa.com

8:30am - 8:35am
Chair Remarks
8:35am - 9:00am
Presentation: Harnessing In-Cell Selection For Small Molecule RNA Targeting
  • Kevin Weeks - Kenan Distinguished Professor of Chemistry, UNC Chapel Hill
9:00am - 9:25am
Presentation: Programmable snoRNA-mediated Protein Localization Inside and Outside Cells
  • Tao Pao - Professor of Biochemistry & Molecular Biology, Univerity of Chicago
9:25am - 9:50am
Presentation: Leveraging Covalent Chemistry to Achieve RNA Selectivity
9:50am - 10:15am
Presentation: Technology Presentation Opportunity Available

Please contact Jennifer Wickett for more information: Jennifer.Wickett@informa.com

8:30am - 8:35am
Chair Remarks
8:35am - 8:50am
Innovation Presentation: Pioneering taRNA Therapies for Infectious Disease and Beyond
  • Cory Sago - CEO, Amplitude Therapeutics
8:50am - 9:05am
Innovation Presentation: Pioneering brain-specific delivery of antibody-oligo conjugates to treat neurological diseases
  • David Hardwicke - Co-Founder, Aerska
9:05am - 9:20am
Innovation Presentation: Exploring First-In-Class Re-Dosable circRNA For Rare Metabolic Disease
  • Bakhytar Ali - CEO, Amirxa Pharma
9:20am - 9:35am
Presentation: Innovation Presentation Opportunity Available

Please contact Jennifer Wickett for more information: Jennifer.Wickett@informa.com

9:35am - 9:50am
Presentation: Innovation Presentation Opportunity Available

Please contact Jennifer Wickett for more information: Jennifer.Wickett@informa.com

9:50am - 10:15am
Presentation: Innovation Presentation Opportunity Available

Please contact Jennifer Wickett for more information: Jennifer.Wickett@informa.com

Showing 1 of 1 Streams
10:15am - 11:00am
Morning Break
Showing 3 of 3 Streams
11:00am - 11:25am
Presentation: Biocatalytic Approaches to Therapeutic Oligonucleotide Manufacturing
  • Bao Cai, PhD - Executive Director, Process Development, Sarepta Therapeutics
11:25am - 11:50am
Presentation: Process Development and characterization of PMO for AOC drug candidate for Duchenne Dystrophy
11:50am - 12:15pm
Presentation: Overcoming Challenges in Peptide-Oligonucleotide Conjugation (POC): From Lead Optimization through Scale-Up
  • Jun Zhou - Senior Director, Oligonucleotide Medicinal Chemistry, WuXi TIDES
12:15pm - 12:35pm
Panel: Advancing Targeted Delivery Strategies for Oligonucleotide & Next-Gen RNA Therapeutics
  • Annette Bak, Ph.D. - Head of Advanced Drug Delivery, AstraZeneca
11:00am - 11:25am
Presentation: mRNA-based Immunotherapy for Adult Solid Tumors and Paediatric Sarcomas
  • Randall Hyer - Chief Executive Officer, Merlin Biotech
11:25am - 11:50am
Presentation: Pioneering Durable Expression via Modified & Optimized saRNA Therapeutics
  • Joshua McGee - CSO, Keylicon Biosciences
11:50am - 12:15pm
Presentation: Build Once, Run Many: An Adaptable IVT and Purification Platform for Next-Gen RNA
  • Rok Sekirnik - Head Process Development mRNA/pDNA, Sartorius BIA Separations
12:15pm - 12:35pm
Panel: Circular RNA -The Next Frontier in RNA Therapeutics
  • Peter Weinstein - CEO, Circurna
  • Anna-Rose Welch - Editorial and Community Director Advancing RNA, Life Science Connect
11:00am - 12:55pm
Investor Insights: Question Circle
Showing 1 of 1 Streams
12:55pm - 2:10pm
Lunch
Showing 3 of 3 Streams
2:10pm - 2:35pm
Presentation: Targeted Delivery of Oligonucleotides for Neuromuscular Diseases
2:35pm - 3:00pm
Presentation: Intravenous Brain-Penetrant Enzyme Therapy for Mucopolysaccharidosis II
3:00pm - 3:25pm
Presentation: Incorporating AI novel RNAi delivery with enhanced cell and tissue specificity
3:25pm - 3:50pm
Presentation: Technology Presentation Opportunity Available

Please contact Jennifer Wickett for more information: Jennifer.Wickett@informa.com

2:10pm - 2:35pm
Presentation
2:35pm - 3:00pm
Presentation: Pioneering Stabilized Nanoparticles For mRNA Multiroute Delivery
3:00pm - 3:25pm
Presentation: Optimizing mRNA delivery with targeted LNPs for muscle, bone marrow, and immune cell therapies
3:25pm - 3:50pm
Presentation: Light up your LNP workflow with Sunshine and Stunner AF
  • Ben Knappett - Product Manager, Sunny Suite, Unchained Labs
2:10pm - 3:10pm
Pharma Insights Question Circle

An open Q&A session providing attendees the chance to interact with pharma leaders, explore industry perspectives, and discuss strategies for advancing RNA therapeutics from discovery to commercialization.

Showing 1 of 1 Streams
3:50pm - 4:30pm
Afternoon Break
Showing 1 of 1 Streams
4:30pm - 5:30pm
Round Tables
Wednesday, September 23
NextFriday, September 25
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