Agenda - Wednesday, September 17th, 2025 - Main Conference Day One

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Development of Emerging Cell & Gene Therapies

8:55am - 9:00am

Chairperson’s Opening Remarks: Development of Emerging Cell & Gene Therapies

9:00am - 9:30am

Harnessing AI and Machine Learning for the Future of Cell & Gene Therapy Development

How to effectively adopt AI tools in the CGT space
Opportunities for AI and machine learning in process development & manufacturing
Real-world applications of AI in CGT pipeline development
Case study insights on AI-driven innovation

9:30am - 10:00am

Redosable DNA Delivery Systems Designed by Machine Learning

Shashi Murthy - CTO and Co-Founder, Nanite Inc.

10:00am - 10:30am

Revolutionizing Targeted Delivery: Emerging Technologies to Enhance Precision & Minimize Off-Target Effects

Cutting-edge technologies for smarter, more precise therapeutic delivery
Strategies to minimize off-target effects and boost efficacy
Cost-effective enabling innovations for scalable implementation
Optimized engineering approaches for enhanced targeting
Real-world case study showcasing successful applications

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Development of Emerging Cell & Gene Therapies

11:30am - 12:00pm

Leveraging Gene Editing Technologies for Precision and Efficiency in Cell and Gene Therapy Development

Kristy Wood - SVP, Technical Operations, Intellia Therapeutics

12:00pm - 12:30pm

Next-Gen Gene Editing – Pushing Boundaries for Enhanced Therapeutics

Integrating novel editing approaches – base, primer editing etc.
In vivo gene editing
Beyond current limits – emerging solutions for larger, more complex payload
Addressing the gaps of established editing technologies– precision editing, single-strand cutting & beyond
Therapeutic advancements – correcting genetic defects & enhancing therapies
Case study– transitioning to scalable in vivo applications

12:30pm - 1:00pm

Application of Next Generation Editing Technologies

Spotlight Presentation – Calling all Technology Thought Leaders!

Whether you're increasing your company profile, launching a new product or focusing on new business development opportunities, collaborate with us to identify custom solutions to help you reach your goals.

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Development of Emerging Cell & Gene Therapies

2:10pm - 2:15pm

Chairperson’s Opening Remarks: Development of Emerging Cell & Gene Therapies

2:15pm - 2:45pm

Panel Discussion: Viral vs. Non-Viral – The Future of In Vivo Delivery Systems

Join industry experts as we explore the cutting edge of non-viral gene delivery. This dynamic discussion will cover:

The Non-Viral Advantage – Where does it shine over viral vectors?
Beyond the Liver – Innovative delivery routes (brain, tissue-specific targeting).
Next-Gen Delivery Vehicles – How to utilize LNP alternatives (EVs, VLPs etc) and machine learning-powered targeting
Optimizing Payloads – Single vs. combination payload strategies
Analytical & Regulatory Insights – Ensuring safety, efficacy, and consistency
Future Trends – Will in vivo LNP therapies overtake ex vivo approaches?
Collaboration & Acceleration – How can companies drive non-viral innovation?

Where is non-viral delivery headed? Let’s discuss the breakthroughs shaping the future!

2:45pm - 3:15pm

Optimizing LNP Delivery and Non-Viral Vector Manufacturing as Scalable, Redosable Alternatives to Viral Vectors

Weiyi Li - Senior Manager, LNP Formulation, Prime Medicine, Inc.

3:15pm - 3:45pm

Utilizing Next-Gen Delivery Vehicles

Spotlight Presentation – Calling all Technology Thought Leaders!

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Development of Emerging Cell & Gene Therapies

4:30pm - 5:30pm

Panel Discussion: Cell and Gene Therapy CDMO Selection and External Manufacturing Best Practices

Shankar Swaminathan, PhD - Team Lead, Drug Product Development, CMC-Tech Ops, Astellas Institute for Regenerative Medicine
Jeffrey Masten - Senior Vice President CMC, Secretome Therapeutics
Matthew Provencal - Executive Director Gene Therapy BDS Manufacturing, Sarepta

Wednesday, September 17th, 2025 - Main Conference Day OneWednesday, 17 September 2025 - ET (Eastern Time, GMT-05:00)