Unite With the Rare Disease Community to Create Powerful Partnerships, Advance Orphan Therapeutics and Deliver Life-Changing Breakthroughs
The Rare Disease Summit unites stakeholders to accelerate therapeutic innovation for areas of unmet medical need. Gain actionable insights on launch planning, market access, reimbursement strategies and strategic partnerships to optimize rare disease commercialization and elevate patient impact.
Have a profound impact on the Rare Disease Community
While the industry has seen growth and heightened focus around the pursuit of orphan products and rare therapies, we’ve only scratched the surface. Benefit from high-impact content from experts from across the rare disease industry:
Strategic Innovation for Rare Disease Commercialization Success
- Launch rare disease therapies with precision using proven pre-launch and post-launch planning strategies
- Leverage AI and advanced data analytics to improve patient identification engagement, and adherence
- Navigate competitive and underserved markets with tailored go-to-market strategies for rare conditions
- Align cross-functional teams across commercial, market access and patient support for scalable success
- Drive innovation in patient services with high-touch models and personalized patient support programs
Whether you're leading a new product launch, refining your access strategy or scaling patient support, the Rare Disease Summit delivers the strategic insights and peer-tested approaches that you need to succeed in the rare disease space.
Operational Strategy and Market Access Alignment for Rare Disease Leaders
- Engage payers and regulators early to shape favorable access and reimbursement outcomes
- Navigate global vs. U.S. market dynamics with tailored distribution and commercialization models
- Design high-impact patient support programs that meet the unique needs of rare disease populations
- Break down silos across commercial, medical and patient services teams to accelerate performance
The Rare Disease Summit delivers the frameworks and insights needed to optimize execution and ensure therapies reach the right patients—at the right time, whether you're leading commercial strategy, market access or patient services.
Collaborative Leadership Across the Rare Disease Ecosystem
- Participate in sessions across the Rare Disease Summit as well as the Hub East Congress and Patient Assistance and Access event
- Engage with the top pharmaceutical companies that shaping rare disease strategy and commercialization
- Collaborate with patient advocacy organizations to amplify patient voice and improve support programs
- Gain insights from FDA, NIH, and health systems on policy, access, and innovation in rare disease
The Rare Disease Summit is the only event on the market where you’ll hear directly from industry, advocacy, government representatives and thought leaders from across the patient access industry – giving you the holistic perspective needed to lead effectively in this complex space.
Their Passion is RARE: Meet the 2026 Rare Disease Conference Thought Leaders
Attendees will hear directly from those who have designed and led innovative approaches to complex challenges in driving curative progress
See Who You'll Meet at the Rare Disease Summit
Our event is ideal for specialists from rare disease and orphan drug companies seeking breakthrough strategies, invaluable connections and actionable insights with roles in:
Rare Disease
Orphan Drugs
Market Access
Commercial Strategy/Operations
Reimbursement
Early/Expanded Access
Launch Excellence
Product Launch
Portfolio Management/Strategy
Marketing
Development
Patient Advocacy
Payer Strategy
Patient Support/Services
This event will also benefit consultants and solution providers who provide services in the rare disease space.
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Engage Qualified Decision Makers in the Rare Disease Community!
Whether you’re looking to generate quality leads, showcase thought leaders, or reinforce your brand, collaborate with us to identify custom sponsorship opportunities to help you reach your business objectives.
Contact Karen Hanover to learn more at KarenH@informaconnectls.com
Content Corner
Access and Channel Insights
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FAQs
Where and when is Rare Disease Summit held?
Rare Disease Summit takes place March 17-19, 2026 with pre-conference workshops on March 16, at the Sheraton Philadelphia Downtown in Philadelphia, PA. Rare Disease Summit is part of Access USA - Driving the future of patient access.
Who should attend the Rare Disease Summit?
Our event brings together stakeholders across the rare-disease ecosystem: industry leaders, biotech & pharma commercial teams, regulatory and market-access professionals, patient advocacy organisations, payers, and service providers.
What types of sessions will be included?
The agenda at Rare Disease Summit 2026 will cover key topics such as orphan-therapy launch planning, market access and reimbursement strategies, patient-centric commercialisation, strategic partnerships, and stakeholder collaboration (industry + patients + payers + regulators).
Can I access session recordings after the event?
Yes. Attendees will be able to access all sessions and recorded presentations* through Streamly, up to 12 months after the event.
*Pending speaker permissions
Are there sponsorship or exhibiting opportunities?
Yes! Organisations wishing to sponsor or exhibit can contact the event team to explore packages that align with their business objectives and gain access to decision-makers in the rare-disease space.
Who should I contact if I have questions about my registration, sponsorship, or speaking opportunities?
- For speaking opportunities: Nhu Tran (nhu.tran@informa.com)
- For registration & teams: Ruhed Miah (ruhed.miah@informa.com)
- For sponsorship & exhibits: Karen Hanover (karen.hanover@informa.com)